July 12, 2013

For those suffering from heart or lung disease, cancer, systemic infections or other all-too-common conditions, the science of medicine has made extraordinary advances over the past few decades.

June 7, 2013

For those suffering from heart or lung disease, cancer, systemic infections or other all-too-common conditions, the science of medicine has made extraordinary advances over the past few decades. But millions of patients afflicted with an uncommon and little-understood disorder often are consigned to the far margins of medical care, in many cases, for years.

June 27, 2012

A bill passed in the Senate will provide measures to speed up the development of treatments for people who desperately need them.

May 3, 2012

Drug makers could strike big with new treatments for rare diseases, according to a new report by a market research firm.

February 25, 2011

More than 400 drugs are in late-stage clinical development or awaiting Food and Drug Administration approval as treatments for rare diseases, according to a report by the drug industry lobby.

February 23, 2010

A nationwide, patient-centered health management organization, serving patients with rare, ultra-orphan disorders, is supporting the...