August 20, 2014

The Food and Drug Administration has approved Cerdelga (eliglustat) for the treatment of adult patients with the Type 1 form of Gaucher disease.

October 2, 2012

An experimental drug for treating a rare genetic disease appears effective, according to a late-stage clinical trial.

May 3, 2012

Drug makers could strike big with new treatments for rare diseases, according to a new report by a market research firm.

May 2, 2012

The Food and Drug Administration has approved a new treatment for a rare genetic disorder that affects 10,000 people worldwide.

November 23, 2011

British drug maker Shire is looking to make a biotech drug for a rare genetic disorder at a new manufacturing plant in Massachusetts.

April 7, 2011

Pfizer is partnering with San Diego biotech company Zacharon Pharmaceuticals to develop treatments for rare genetic disorders Zacharon said Thursday.

February 25, 2011

The Food and Drug Administration has declined to approve a biologic treatment for a rare genetic disorder by Israeli drug maker Protalix Biotherapeutics, Protalix said Friday.

July 7, 2010

Generic drug maker Hospira will fill and package several drugs for Genzyme, according to published...

May 23, 2010

Biotech company Genzyme will pay $175 million to the federal government as part of an...

February 25, 2010

The Food and Drug Administration has approved a new drug for treating a rare genetic...